1. A xenotransplantation model for reactivation of paternal UBE3A using human-specific antisense oligonucleotides.
Smeenk H,
Lendemeijer B,
Buurma MG, Forgione MA,
Slump DE, Monshouwer RA, Wallaard I,
Mientjes EJ, Hoogendijk WJG,
Elgersma Y,
de Vrij FMS,
Kushner SA
in Scientific reports 2026
